Sickle Cell Disease Solution: Gene Therapy Tips for Healthy Children

genomics is a field that impact our everyday life more than we may recognize . The Holocene Students talk Science event form by Cold Spring Harbor Laboratorys ( CSHLs ) DNA Learning Center foreground the real_number - universe impact of genomics . One of the have guest , Victoria Gray , share her personal experience with Sickle cell disease and CRISPR gene - editing technology . She is the first person ever treat with CRISPR and bring_around of sickle cell disease , a familial disorder that cause severe pain.

Gray 's narrative is one of hope , as she discourse how CRISPR technology could potentially better the life of person with sickle cell disease . At the event , she spoke not only to CSHL scientist but also to doctor , patient , and family from the New York City metro area , aim to include group historically exclude from scientific discourse . The event have a divers audience , emphasizing the importance of delivery different position into scientific conversations.

In a offprint development , a South Jersey student name Austin Louis has found new hope with Gene therapy at the Children 's Hospital of Philadelphia ( CHOP ) . Louis , who hour_angle sickle cell disease , has been unable to play sport due to the torment pain cause by the familial disorder . However , with the gene therapy research at CHOP , there be newfound hope for person like Louis to lead a pain - free life.

Dr. Tim Olson from CHOP describe the gene therapy as groundbreaking and a significant discovery in sickle cell disease care . The therapy involve manipulate the patient 's root cell to normalize the blood and prevent the complication associate with sickle cell disease . For Louis , this therapy means undergo chemotherapy before receive the graft of his edit root cell , lead to a life beyond sickle cell disease.

The research at CHOP has show promise consequence , with 96 % of patient experience pain - free time_period of at least a year after receive the gene therapy . For person like Austin Louis and Victoria Gray , gene therapy offer hope for a future free from the pain and restriction enforce by sickle cell disease . As promotion in genomics and gene therapy continue to advancement , More person may benefit from life - change treatment in the future.